Image

Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program

Monitoring program for fatty acid oxidation disorders in clinic.

Recruiting
All
Phase N/A

Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) are conditions where the body struggles to use certain fats for energy. This study is about checking the long-term safety of people with LC-FAOD, especially focusing on women who are pregnant or breastfeeding. The study will last up to 10 years, gathering information from people who have been treated with a special fat called triheptanoin in the past or in other studies. Triheptanoin is not given directly by this study; instead, it can be accessed commercially or through other special programs if available in their country.

  • The study lasts up to 10 years and involves both adults and children.
  • Participants will be monitored by their doctors and may or may not use triheptanoin during the study.
  • People with confirmed LC-FAOD willing to follow study rules and provide necessary permissions can participate.

Pregnant women can continue in the study to help understand how LC-FAOD affects pregnancy. However, if they have another disease or condition that the study doctor thinks might cause problems, they might not be able to join or stay in the study.

Study details
    Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)

NCT04632953

Ultragenyx Pharmaceutical Inc

16 February 2025

Step 1 Get in touch with the nearest study center
What happens next?
  • You can expect the study team to contact you via email or phone in the next few days.
  • Sign up as volunteer  to help accelerate the development of new treatments and to get notified about similar trials.

You are contacting

Investigator Avatar

Primary Contact

site

  Other languages supported:

FAQs

Learn more about clinical trials

What is a clinical trial?

A clinical trial is a study designed to test specific interventions or treatments' effectiveness and safety, paving the way for new, innovative healthcare solutions.

Why should I take part in a clinical trial?

Participating in a clinical trial provides early access to potentially effective treatments and directly contributes to the healthcare advancements that benefit us all.

How long does a clinical trial take place?

The duration of clinical trials varies. Some trials last weeks, some years, depending on the phase and intention of the trial.

Do I get compensated for taking part in clinical trials?

Compensation varies per trial. Some offer payment or reimbursement for time and travel, while others may not.

How safe are clinical trials?

Clinical trials follow strict ethical guidelines and protocols to safeguard participants' health. They are closely monitored and safety reviewed regularly.
Add a private note
  • abc Select a piece of text.
  • Add notes visible only to you.
  • Send it to people through a passcode protected link.