Duchenne muscular dystrophy (DMD) is a condition that makes muscles weak. This study wants to learn more about a type of antibody, called anti-AAV8, in boys with DMD. Antibodies are like soldiers in our body that fight invaders like viruses. AAV8 stands for adeno-associated virus serotype 8, which is a type of virus that can be used in gene therapy. Gene therapy is a treatment that tries to fix the genes that cause DMD.
To join the study, boys need to be under 12 years old, have DMD, and their parents must agree. Boys who have already had gene therapy cannot join. The study involves:
- A phone or video call to agree and share medical history.
- A home visit to take a blood sample.
- A final phone or video call to discuss the test results.
The study helps researchers find boys who might be good for future gene therapy trials. It’s important to know there is no treatment or payment in this study. It's just to gather information. There are no big risks involved, but there will be a blood test.